Science and Health
After Receiving a Custom Experimental Medicine, a Teen With a Rare Genetic Disorder Walked on His Own for the First Time
The patient's genetic disorder causes frequent seizures and developmental delays. His progress, along with that of another boy who received a similar personalized treatment, highlights the promise—and challenges—of tailor-made drugs
Source: Smithsonian Smart NewsImage credit: Smithsonian Smart NewsSource published Aug 33 min readBrightSide page reviewed Aug 3
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